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Carvalho LS, Xu J, Pearson RA, Smith AJ, Bainbridge JW, Morris LM, Fliesler SJ, Ding XQ, Ali RR (2011). Long-term and age-dependent restoration of visual function in a mouse model of CNGB3-associated achromatopsia following gene therapy. Hum Mol Genet 20: 3161-75. >>

Colella P, Iodice C, Di Vicino U, Annunziata I, Surace EM, Auricchio A (2011). Non-erythropoietic erytropoietin derivates protect from light-induced and genetic photoreceptor degeneration. Hum Mol Genet 20: 2251-2262. >>

Karali M, Manfredi A, Puppo A, Marrocco E, Gargiulo A, Allocca MC, Della Corte M, Rossi S, Giunti M, Bacci ML, Simonelli F, Surace EM, Banfi S, Auricchio A (2011). microRNA-restricted transgene expression in the retina. PLoS ONE 6: e22166. >>

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Mussolino C, Sanges D, Marrocco E, Bonetti C, Di Vicino U, Marigo V, Auricchio A, Meroni G, Surace EM (2011). Zinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosa. EMBO Mol Med 3: 1-11. >>

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Tan MH, Smith AJ, Pawlyk B, Xu X, Liu X, Bainbridge JB, Basche M, McIntosh J, Tran HV, Nathwani A, Li T, Ali RR (2009). Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors. Hum Mol Genet 18: 2099-2114. >>